LAURA FIONDA

Dottoressa di ricerca

ciclo: XXXV



Titolo della tesi: Neuromuscular imaging as a biomarker for disease diagnosis and progression

Preface Diagnosis of neuromuscular diseases (NMDs) was historically made on the basis of the clinical picture, neurological examination and neurophysiological and pathological studies. Over the last 20 years, the development of innovative imaging methods has shown the possibility to study nerve and muscle structures in detail, analyse the severity and distribution of damage and identify specific patterns of involvement [1,2], making a strong contribution to early diagnosis and, therefore, to early treatment of patients. In general, neuromuscular diseases are rare diseases, and a high level of standardization of imaging methods is required to compare individual patient data across different imaging centres. To achieve this target, standardized evaluation and innovative methods of quantification have emerged [3]. Moreover, emerging innovative therapies for hereditary and acquired diseases have renewed the interest in studying the natural history of these diseases, the degree of damage progression and, finally, the therapeutic response [4], topics to which imaging techniques have made a useful contribution. On these bases, both high-resolution ultrasound (HRUS) and magnetic resonance imaging (MRI) have progressively become essential tools to support the clinician in diagnosing peripheral neuropathies and muscle diseases [5]. HRUS may provide information about morphological abnormalities in nerve and muscles, contributing, together with EDx study, in the diagnosis of neuropathies and myopathies. . HRUS enhances the ability to detect focal nerve entrapment, as well as pathological nerve enlargements in genetic and acquired neuropathies [6]. To date, US has been introduced as supportive diagnostic criteria for CIDP diagnosis [7]. Furthermore, muscle fibrosis and fat replacement can potentially be detected by HRUS and used as a biomarker for muscular dystrophies and motor neuron disorders [8,9]. Sometimes, in the clinical practice, it can also guide needle placement for therapeutic injections (i.e. botulinum toxin), for electromyographic examination and suggest the site for muscle/nerve biopsy. Last, but not least, HRUS is inexpensive and well tolerated. Potential limitations of HRUS include an inability to image deeper structures and its reliability and replicability (it is frequently based on an operator-dependent interpretation) especially among different centres. MRI has already demonstrated to be a useful tool for the diagnosis of a wide variety of primary muscle disorders including both acquired and inherited myopathies. It can provide complementary information to clinical, histologic, genetic, and laboratory findings for the identification of specific muscular tissue alterations [10]. Muscle MRI allows the identification of oedema and fat replacement of muscle tissue through conventional MRI sequences such as T1-weighted and STIR and can be helpful for diagnosis of inherited and inflammatory myopathies that exhibit distinctive patterns of muscle involvement, especially when they are not yet clinically observable [11]. Muscle MRI can also increase sensitivity and specificity of muscle biopsy; finally, there is growing interest in using muscle MRI to assess disease progression and evolution overtime, also for monitoring the response to treatment both in clinical trials and in clinical practice. Peripheral nerve MRI can add information especially about nerve roots and deep nerves that cannot be studied through US, and for alterations that could be detected with post-contrast acquisitions [7,12]. However, high costs and low availability do not allow an extensive use of MRI in clinical practice. To date, even if diagnostic role of HRUS and MRI in neuromuscular diseases is well known [3], less is known about modification of nerves and muscles over-time in different disorders, also with respect to treatments, and about comparison between the two techniques. This dissertation summarizes the results obtained during these years in our centre for neuromuscular and rare diseases, focused on diagnosis and follow-up of inherited and acquired rare neuromuscular diseases, as well as comparison between the US and MRI techniques. It is divided in four sections: the first three about published results and the third one about ongoing and future projects.

Produzione scientifica

11573/1705210 - 2024 - Chronic inflammatory demyelinating polyneuropathy and HEV antibody status: A case-control study from Lazio, Italy
Moret, Federica; Spada, Enea; Ceccanti, Marco; Libonati, Laura; D’Andrea, Edoardo; Villano, Umbertina; Madonna, Elisabetta; Chionne, Paola; Carocci, Alberto; Pisani, Giulio; Fionda, Laura; Antonini, Giovanni; Petrucci, Antonio; Bruni, Roberto; Rita Ciccaglione, Anna; Taliani, Gloria; Rivano Capparuccia, Marco; Nobile-Orazio, Eduardo; Inghilleri, Maurizio; Cambieri, Chiara - 01a Articolo in rivista
rivista: JOURNAL OF THE NEUROLOGICAL SCIENCES (Elsevier BV:PO Box 211, 1000 AE Amsterdam Netherlands:011 31 20 4853757, 011 31 20 4853642, 011 31 20 4853641, EMAIL: nlinfo-f@elsevier.nl, INTERNET: http://www.elsevier.nl, Fax: 011 31 20 4853598) pp. - - issn: 0022-510X - wos: (0) - scopus: 2-s2.0-85188011351 (0)

11573/1697446 - 2023 - Eculizumab for myasthenic exacerbation during treatment with immune-checkpoint inhibitors
Fionda, Laura; Rossini, Elena; Lauletta, Antonio; Leonardi, Luca; Tufano, Laura; Costanzo, Rocco; Marchetti, Paolo; Salvetti, Marco; Garibaldi, Matteo; Morino, Stefania; Antonini, Giovanni - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (-Springer-Verlag Italia -Masson SPA:via Flli Bressan 2, I 20126 Milan Italy:011 39 02 27074286, EMAIL: aboonamenti@masson.it, INTERNET: http://www.masson.it, Fax: 011 39 02 27074210) pp. - - issn: 1590-1874 - wos: (0) - scopus: 2-s2.0-85180188927 (0)

11573/1684211 - 2023 - Comparison of quantitative muscle ultrasound and whole-body muscle MRI in facioscapulohumeral muscular dystrophy type 1 patients
Fionda, Laura; Vanoli, Fiammetta; Di Pasquale, Antonella; Leonardi, Luca; Morino, Stefania; Merlonghi, Gioia; Lauletta, Antonio; Alfieri, Girolamo; Costanzo, Rocco; Tufano, Laura; Rossini, Elena; Bucci, Elisabetta; Grossi, Andrea; Tupler, Rossella; Salvetti, Marco; Garibaldi, Matteo; Antonini, Giovanni - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (-Springer-Verlag Italia -Masson SPA:via Flli Bressan 2, I 20126 Milan Italy:011 39 02 27074286, EMAIL: aboonamenti@masson.it, INTERNET: http://www.masson.it, Fax: 011 39 02 27074210) pp. - - issn: 1590-1874 - wos: WOS:001005822800003 (1) - scopus: 2-s2.0-85163104338 (1)

11573/1688739 - 2023 - Prominent mitochondrial pathology in a case of refractory dermatomyositis: coincidence or concause?
Lauletta, Antonio; De Carolis, Lanfranco; Teresi, Valentina; Fionda, Laura; Leonardi, Luca; Ceccanti, Marco; Costanzo, Rocco; Rossini, Elena; Tufano, Laura; Merlonghi, Gioia; Morino, Stefania; Garibaldi, Matteo - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (Springer-Verlag Italia Srl:via Decembrio 28, 20137 Milan Italy:011 39 2 5425971, EMAIL: riccardi@springer.it, Fax: 011 39 2 55193360) pp. - - issn: 1590-3478 - wos: WOS:001060221000001 (0) - scopus: 2-s2.0-85168927577 (0)

11573/1686111 - 2023 - Quantitative sensory testing and skin biopsy findings in late‐onset ATTRv pre‐symptomatic carriers: relationships with predicted time of disease onset (PADO)
Leonardi, Luca; Costanzo, Rocco; Forcina, Francesca; Morino, Stefania; Antonini, Giovanni; Salvetti, Marco; Luigetti, Marco; Romano, Angela; Primiano, Guido; Guglielmino, Valeria; Fionda, Laura; Garibaldi, Matteo; Lauletta, Antonio; Rossini, Elena; Tufano, Laura; Ceccanti, Marco; Esposito, Nicoletta; Falco, Pietro; Di Pietro, Giuseppe; Truini, Andrea; Galosi, Eleonora - 01a Articolo in rivista
rivista: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM (Woodland Publishers Incorporated:69 Murray Street:New York, NY 10007:(212)566-4294, EMAIL: woodlpub@pipeline.com, INTERNET: http://www.elsevier.nl, Fax: (212)406-6496) pp. - - issn: 1085-9489 - wos: WOS:001049309000001 (2) - scopus: 2-s2.0-85168337501 (2)

11573/1678194 - 2023 - Safety and efficacy of rozanolixizumab in patients with generalised myasthenia gravis (MycarinG): a randomised, double-blind, placebo-controlled, adaptive phase 3 study
Vera, Bril; Artur, Drużdż; Julian, Grosskreutz; Ali A, Habib; Renato, Mantegazza; Sabrina, Sacconi; Kimiaki, Utsugisawa; John, Vissing; Tuan, Vu; Marion, Boehnlein; Ali, Bozorg; Maryam, Gayfieva; Bernhard, Greve; Franz, Woltering; Kaminski, ; J Angela Genge, Henry; Massie, Rami; Berube, Maxime; Bril, Vera; Daniyal, Lubna; Mannan, Shabber; Ng, Eduardo; Rohan Raghu Raman, Ritesh; Sarpong, Evelyn; Alcantara, Monica; Dionne, Annie; Siddiqi, Zaeem; Blackmore, Derrick; Hussain, Faraz; Matte, Genevieve; Botez, Stephan; Tyblova, Michaela; Jakubikova, Michala; Junkerova, Jana; Vissing, John; Witting, Nanna; Holm-Yildiz, Sonja; Stemmerik, Mads; Andersen, Henning; Obál, Izabella; Solé, Guilhem; Mathis, Stéphane; Violleau, Marie-Hélène; Tranchant, Christine; Messai, Sihame; Chanson, Jean-Baptiste; Nadaj-Pakleza, Aleksandra; Verloes, Arnaud; Zaidi, Leila; Sacconi, Sabrina; Gambella, Manuela; Cavalli, Michele; Stojkovic, Tanya; Demeret, Sophie; Le Guennec, Loic; Querin, Giorgia; Weiss, Nicolas; Masingue, Marion; Magy, Laurent; Ghorab, Karima; Rukhadze, Ia; Tsiskaridze, Alexander; Janelidze, Marina; Margania, Temur; Then Bergh, Florian; Hänsel, Eike; Kalb, Andrea; Meilick, Bianca; Reuschel, Mandy; Teußer, Lars-Malte; Unterlauft, Astrid; Goedel, Clemens; Hagenacker, Tim; Totzeck, Andreas; Stolte, Benjamin; Blaes, Franz; Bindler, Christine; Tsoutsikas, Vasilios; Roediger, Annekathrin; Geis, Christian; Schmidt, Jens; Zschüntzsch, Jana; Schwarz, Margret; Meyer, Stefanie; Kummer, Karsten; Glaubitz, Stefanie; Zeng, Rachel; Wiendl, Heinz; Klotz, Luisa; Lammerskitten, Anna; Lünemann, Jan; Diószeghy, Péter; Mantegazza, Renato; Maggi, Lorenzo; Rinaldi, Elena; Gastaldi, Matteo; Mazzacane, Federico; Businaro, Pietro; Iorio, Raffaele; Antonini, Giovanni; Fionda, Laura; Rinaldi, Rita; Rossi, Simone; Habetswallner, Francesco; Tuccillo, Francesco; Umehara, Haruna; Uenaka, Eiko; Takahashi, Masanori; Higashi, Keiko; Kinoshita, Makoto; Yoneda, Emika; Nakamura, Noriko; Fujita, Saeka; Kubota, Tomoya; Ono, Masami; Yamamoto, Sana; Hatano, Taku; Oikoshi, Kazuki; Yokoyama, Kazumasa; Oji, Yutaka; Tomizawa, Yuji; Uzawa, Akiyuki; Yasuda, Manato; Akita, Sachiko; Ozawa, Yukiko; Onishi, Yosuke; Takaki, Miki; Yamada, Hiromi; Minemoto, Kanako; Sanko, Miki; Izawa, Nanae; Nakayama, Mayumi; Masuda, Masayuki; Tsuji, Rune; Ido, Nobuhiro; Hyodo, Yumi; Okubo, Yoshihiko; Minohara, Akiko; Haraguchi, Nana; Naito, Makiko; Yoshida, Seiko; Fukushige, Yuri; Tsujino, Akira; Nagaoka, Atsushi; Miyazaki, Teiichiro; Yoshimura, Shunsuke; Hirayama, Takuro; Shima, Tomoaki; Okamoto, Naoko; Matsumoto, Riki; Sekiguchi, Kenji; Ueda, Takehiro; Chihara, Norio; Kirimura, Mari; Sunagawa, Emi; Suzuki, Ayaka; Suzuki, Shigeaki; Wada, Aozora; Ishizuchi, Kei; Suzuki, Yasushi; Yata, Mitsuo; Komatsu, Yuka; Tsukita, Kenichi; Watanabe, Genya; Sato, Kazuki; Kawasaki, Emiko; Yamamoto, Naoki; Ono, Hirohiko; Tsuda, Tomoko; Ohashi, Shigeki; Utsugisawa, Kimiaki; Fujisawa, Yuka; Yokota, Yumiko; Nagane, Yuriko; Ayumi, Kameda; Takematsu, Yuka; Naito, Hiroyuki; Kuwada, Kumiko; Rejdak, Konrad; Szklener, Sebastian; Kitowska, Monika; Derkacz, Kandyda; Drużdż, Artur; Berkowicz, Tomasz; Budzinska, Paulina; Halas, Marek; Zaslavskiy, Leonid; Skornyakova, Evgeniya; Kotov, Sergey; Novikova, Ekaterina; Sidorova, Olga; Goldobin, Vitalii; Alekseeva, Tatiana; Isabekova, Patimat; Malkova, Nadezhda; Korobko, Denis; Djordjevic, Gordana; Stojanov, Aleksandar; Peric, Stojan; Lavrnic, Dragana; Bozovic, Ivo; Palibrk, Aleksa; Casasnovas, Carlos; Nedkova-Hristova, Velina; Vidal Fernández, Nuria; Cortés Vicente, Elena; Querol Gutiérrez, Luis; Salvadó Figueras, Maria; Canovas Segura, Anna; Juntas Morales, Raúl; Sanchez Tejerina, Daniel; Saiz, Albert; Blanco Morgado, Yolanda; Llufriú Durán, Sara; Sepúlveda Gázquez, María; María Martínez Hernández, Eugenia; Gutiérrez Gutiérrez, Gerardo; Iniesta, Paqui; Meca Lallana, José; Guo, Yuh-Cherng; Chiu, Hou-Chang; Yeh, Jiann-Horng; Hui Chen, Ya; Fen Lee, Me - 01a Articolo in rivista
rivista: LANCET NEUROLOGY (Lancet Publishing Group) pp. 383-394 - issn: 1474-4422 - wos: WOS:001033003300001 (0) - scopus: 2-s2.0-85152149330 (0)

11573/1659088 - 2022 - Muscle MRI in immune-mediated necrotizing myopathy (IMNM). implications for clinical management and treatment strategies
Fionda, Laura; Lauletta, Antonio; Leonardi, Luca; Perez, Jorge Alonso; Morino, Stefania; Merlonghi, Gioia; Alfieri, Girolamo; Costanzo, Rocco; Tufano, Laura; Vanoli, Fiammetta; Rossini, Elena; Vigo, Eduard Gallardo; Tartaglione, Tommaso; Salvetti, Marco; Antonini, Giovanni; Diaz-Manera, Jordi; Garibaldi, Matteo - 01a Articolo in rivista
rivista: JOURNAL OF NEUROLOGY (Springer Verlag Germany:Tiergartenstrasse 17, D 69121 Heidelberg Germany:011 49 6221 3450, EMAIL: g.braun@springer.de, INTERNET: http://www.springer.de, Fax: 011 49 6221 345229) pp. 1-16 - issn: 0340-5354 - wos: WOS:000878454300001 (2) - scopus: 2-s2.0-85141173584 (2)

11573/1659089 - 2022 - Distal upper limb involvement in myasthenia-myositis association
Lauletta, Antonio; Fionda, Laura; Merlonghi, Gioia; Leonardi, Luca; Morino, Stefania; Bucci, Elisabetta; Tufano, Laura; Alfieri, Girolamo; Costanzo, Rocco; Rossini, Elena; Salvetti, Marco; Antonini, Giovanni; Garibaldi, Matteo - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (-Springer-Verlag Italia -Masson SPA:via Flli Bressan 2, I 20126 Milan Italy:011 39 02 27074286, EMAIL: aboonamenti@masson.it, INTERNET: http://www.masson.it, Fax: 011 39 02 27074210) pp. - - issn: 1590-1874 - wos: WOS:000879322000001 (1) - scopus: 2-s2.0-85146249347 (1)

11573/1661856 - 2022 - Nerve high-resolution ultrasound in a 2-years follow-up of radial nerve palsy related to humeral shaft fractures
Leonardi, Luca; Loreti, Simona; Di Pasquale, Antonella; Fionda, Laura; Vanoli, Fiammetta; Morino, Stefania; Garibaldi, Matteo; Alfieri, Girolamo; Lauletta, Antonio; Salvetti, Marco; Antonini, Giovanni - 01a Articolo in rivista
rivista: JOURNAL OF NEUROSURGICAL SCIENCES (Torino: Edizioni Minerva Medica) pp. - - issn: 1827-1855 - wos: (0) - scopus: (0)

11573/1526240 - 2021 - Changes of clinical, neurophysiological and nerve ultrasound characteristics in CIDP over time: a 3-year follow-up
Fionda, L.; Di Pasquale, A.; Morino, S.; Leonardi, L.; Vanoli, F.; Loreti, S.; Garibaldi, M.; Lauletta, A.; Alfieri, G.; Bucci, E.; Salvetti, M.; Antonini, G. - 01a Articolo in rivista
rivista: JOURNAL OF NEUROLOGY (Springer Verlag Germany:Tiergartenstrasse 17, D 69121 Heidelberg Germany:011 49 6221 3450, EMAIL: g.braun@springer.de, INTERNET: http://www.springer.de, Fax: 011 49 6221 345229) pp. - - issn: 0340-5354 - wos: WOS:000622676100003 (11) - scopus: 2-s2.0-85101846564 (11)

11573/1603046 - 2021 - Muscle magnetic resonance imaging in myotonic dystrophy type 1 (DM1): Refining muscle involvement and implications for clinical trials
Garibaldi, M.; Nicoletti, T.; Bucci, E.; Fionda, L.; Leonardi, L.; Morino, S.; Tufano, L.; Alfieri, G.; Lauletta, A.; Merlonghi, G.; Perna, A.; Rossi, S.; Ricci, E.; Alonso Perez, J.; Tartaglione, T.; Petrucci, A.; Pennisi, E. M.; Salvetti, M.; Cutter, G.; Diaz-Manera, J.; Silvestri, G.; Antonini, G. - 01a Articolo in rivista
rivista: EUROPEAN JOURNAL OF NEUROLOGY (Lippincott, Williams & Wilkins:530 Walnut Street:Philadelphia, PA 19106:(800)638-3030, (301)223-2300, EMAIL: orders@lww.com, INTERNET: http://www.lww.com, Fax: (301)223-2320, (301)223-2320) pp. - - issn: 1351-5101 - wos: WOS:000726637400001 (6) - scopus: 2-s2.0-85120489892 (6)

11573/1558042 - 2021 - Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT). a multicentre, randomised, placebo-controlled, phase 3 trial
Howard, J. F.; Bril, V.; Vu, T.; Karam, C.; Peric, S.; Margania, T.; Murai, H.; Bilinska, M.; Shakarishvili, R.; Smilowski, M.; Guglietta, A.; Ulrichts, P.; Vangeneugden, T.; Utsugisawa, K.; Verschuuren, J.; Mantegazza, R.; De Bleeker, J.; De Koning, K.; De Mey, K.; De Pue, A.; Mercelis, R.; Wyckmans, M.; Vinck, C.; Wagemaekers, L.; Baets, J.; Ng, E.; Shabanpour, J.; Daniyal, L.; Mannan, S.; Katzberg, H.; Genge, A.; Siddiqi, Z.; Junkerova, J.; Horakova, J.; Reguliova, K.; Tyblova, M.; Jurajdova, I.; Novakova, I.; Jakubikova, M.; Pitha, J.; Vohanka, S.; Havelkova, K.; Horak, T.; Bednarik, J.; Horakova, M.; Meisel, A.; Remstedt, D.; Heibutzki, C.; Kohler, S.; Hoffman, S.; Stascheit, F.; Vissing, J.; Zafirakos, L.; Khatri, K. K.; Autzen, A.; Godtfeldt Stemmerik, M. P.; Andersen, H.; Attarian, S.; Tsiskaridze, A.; Rozsa, C.; Jakab, G. M.; Toth, S.; Szabo, G.; Bors, D.; Szabo, E.; Campanella, A.; Vanoli, F.; Frangiamore, R.; Antozzi, C.; Bonanno, S.; Maggi, L.; Giossi, R.; Sacca, F.; Marsili, A.; Imbriglio, T.; Antonini, G.; Alfieri, G.; Morino, S.; Garibaldi, M.; Fionda, L.; Leonardi, L.; Konno, S.; Uzawa, A.; Sakuma, K.; Watanabe, C.; Ozawa, Y.; Yasuda, M.; Onishi, Y.; Samukawa, M.; Tsuda, T.; Suzuki, Y.; Ishida, S.; Watanabe, G.; Takahashi, M.; Nakamura, H.; Sugano, E.; Kubota, T.; Imai, T.; Mari, Suzuki.; Mori, A.; Yamamoto, D.; Ikeda, K.; Hisahara, S.; Masuda, M.; Takaki, M.; Minemoto, K.; Ido, N.; Naito, M.; Okubo, Y.; Sugimoto, T.; Takematsu, Y.; Kamei, A.; Shimizu, M.; Naito, H.; Nomura, E.; Van Heur, M.; Peters, A.; Tannemaat, M.; Ruiter, A.; Keene, K.; Halas, M.; Szczudlik, A.; Pinkosz, M.; Frasinska, M.; Zwolinska, G.; Kostera-Pruszczyk, A.; Golenia, A.; Szczudlik, P.; Szczechowski, L.; Marek, E.; Poverennova, I.; Urtaeva, L.; Kuznetsova, N.; Romanova, T.; Nadezhda, M.; Lapochka, E.; Korobko, D.; Vergunova, I.; Melnikova, A.; Bulatova, E.; Antipenko, E.; Bozovic, I.; Lavrnic, D.; Rakocevic Stojanovic, V.; Beydoun, S.; Akhter, S.; Malekniazi, A.; Darki, L.; Pimentel, N.; Cannon, V.; Chopra, M.; Traub, R.; Mozaffar, T.; Turner, I.; Habib, A.; Goyal, N.; Kak, M.; Velasquez, E.; Lam, L.; Suresh, N.; Farias, J.; Jones, S.; Wagoner, M.; Eggleston, D.; Bertorini, T.; Benzel, C.; Henegar, R.; Pillai, R.; Bharavaju-Sanka, R.; Paiz, C.; Jackson, C.; Ruzhansky, K.; Dimitrova, D.; Visser, A.; Chahin, N.; Levine, T.; Lisak, R.; Jia, K.; Mada, F.; Bernitsas, E.; Pasnoor, M.; Roath, K.; Colgan, S.; Currence, M.; Heim, A.; Barohn, R.; Dimachkie, M.; Statland, J.; Jawdat, O.; Jabari, D.; Farmakidis, C.; Gilchrist, J.; Li, Y.; Caristo, I.; Hastings, D.; Anthony Morren, J.; Weiss, M.; Muppidi, S.; Nguyen, T.; Welsh, L.; So, Y.; Pulley, M.; Bailey, C.; Smith, L.; Berger, A.; Sahagian, G.; Camberos, Y.; Frishberg, B. - 01a Articolo in rivista
rivista: LANCET NEUROLOGY (Lancet Publishing Group) pp. 526-536 - issn: 1474-4422 - wos: WOS:000687268300012 (145) - scopus: 2-s2.0-85107960986 (146)

11573/1590182 - 2021 - High-resolution ultrasound of peripheral nerves in late-onset hereditary transthyretin amyloidosis with polyneuropathy: similarities and differences with CIDP
Leonardi, L.; Di Pietro, G.; Di Pasquale, A.; Vanoli, F.; Fionda, L.; Garibaldi, M.; Galosi, E.; Alfieri, G.; Lauletta, A.; Morino, S.; Salvetti, M.; Truini, A.; Antonini, G. - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (-Springer-Verlag Italia -Masson SPA:via Flli Bressan 2, I 20126 Milan Italy:011 39 02 27074286, EMAIL: aboonamenti@masson.it, INTERNET: http://www.masson.it, Fax: 011 39 02 27074210) pp. - - issn: 1590-1874 - wos: WOS:000720711500001 (3) - scopus: 2-s2.0-85119324020 (4)

11573/1558014 - 2021 - Skin biopsy and quantitative sensory assessment in an Italian cohort of ATTRv patients with polyneuropathy and asymptomatic carriers: possible evidence of early non-length dependent denervation
Leonardi, Luca; Galosi, Eleonora; Vanoli, Fiammetta; Fasolino, Alessandra; Di Pietro, Giuseppe; Luigetti, Marco; Sabatelli, Mario; Fionda, Laura; Garibaldi, Matteo; Alfieri, Girolamo; Lauletta, Antonio; Morino, Stefania; Salvetti, Marco; Truini, Andrea; Antonini, Giovanni - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (-Springer-Verlag Italia -Masson SPA:via Flli Bressan 2, I 20126 Milan Italy:011 39 02 27074286, EMAIL: aboonamenti@masson.it, INTERNET: http://www.masson.it, Fax: 011 39 02 27074210) pp. - - issn: 1590-1874 - wos: WOS:000668063500007 (8) - scopus: 2-s2.0-85109136497 (9)

11573/1529657 - 2021 - Post-intervention Status in Patients With Refractory Myasthenia Gravis Treated With Eculizumab During REGAIN and Its Open-Label Extension
R., Mantegazza; G. I., Wolfe; S., Muppidi; H., Wiendl; K. P., Fujita; F. L., O'brien; H. D. E., Booth; J. F., Howard; Gabriel Mazia, Claudio; Wilken, Miguel; Barroso, Fabio; Saba, Juliet; Rugiero, Marcelo; Bettini, Mariela; Chaves, Marcelo; Vidal, Gonzalo; Dalila Garcia, Alejandra; De Bleecker, Jan; Van Den Abeele, Guy; De Koning, Kathy; De Mey, Katrien; Mercelis, Rudy; Mahieu, Délphine; Wagemaekers, Linda; Van Damme, Philip; Depreitere, Annelies; Schotte, Caroline; Smetcoren, Charlotte; Stevens, Olivier; Van Daele, Sien; Vandenbussche, Nicolas; Vanhee, Annelies; Verjans, Sarah; Vynckier, Jan; D'hont, Ann; Tilkin, Petra; Alves De Siqueira Carvalho, Alzira; Dias Brockhausen, Igor; Feder, David; Ambrosio, Daniel; Lovasamela César, Gabor; Paula Melo, Ana; Martins Ribeiro, Renata; Rocha, Rosana; Bezerra Rosa, Bruno; Veiga, Thabata; Augusto Da Silva, Luiz; Santos Engel, Murilo; Gonçalves Geraldo, Jordana; Da Penha Ananias Morita, Maria; Nogueira Coelho, Erica; Paiva, Gabriel; Pozo, Marina; Prando, Natalia; Dada Martineli Torres, Debora; Fernanda Butinhao, Cristiani; Duran, Gustavo; Augusto Suriane Fialho, Tomás; Cristina Gomes Da Silva, Tamires; Otavio Maia Gonçalves, Luiz; Eduardo Pazetto, Lucas; Renata Cubas Volpe, Luciana; Souza Duca, Luciana; Andrégheller Friedrich, Maurício; Guerreiro, Alexandre; Guerreiro, Alexandre; Mohr, Henrique; Pereira Martins, Maurer; Da Cruz Pacheco, Daiane; Ferreira, Luciana; Paula Macagnan, Ana; Pinto, Graziela; De Cassia Santos, Aline; Souza Bulle Oliveira, Acary; Carolina Amaral De Andrade, Ana; Annes, Marcelo; Duarte Silva, Liene; Cavalcante Lino, Valeria; Pinto, Wladimir; Assis, Natália; Carrara, Fernanda; Miranda, Carolina; Souza, Iandra; Fernandes, Patrícia; Siddiqi, Zaeem; Phan, Cecile; Narayan, Jeffrey; Blackmore, Derrick; Mallon, Ashley; Roderus, Rikki; Watt, Elizabeth; Vohanka, Stanislav; Bednarik, Josef; Chmelikova, Magda; Cierny, Marek; Toncrova, Stanislava; Junkerova, Jana; Kurkova, Barbora; Reguliova, Katarina; Zapletalova, Olga; Pitha, Jiri; Novakova, Iveta; Tyblova, Michaela; Jurajdova, Ivana; Wolfova, Marcela; Andersen, Henning; Harbo, Thomas; Vinge, Lotte; Krogh, Susanne; Mogensen, Anita; Vissing, John; Højgaard, Joan; Witting, Nanna; Mette Ostergaard Autzen, Anne; Pedersen, Jane; Erälinna, Juha-Pekka; Laaksonen, Mikko; Oksaranta, Olli; Harrison, Tuula; Eriksson, Jaana; Rozsa, Csilla; Horvath, Melinda; Lovas, Gabor; Matolcsi, Judit; Jakab, Gedeonne; Szabo, Gyorgyi; Jakab, Gedeonne; Szabadosne, Brigitta; Vecsei, Laszlo; Dezsi, Livia; Varga, Edina; Konyane, Monika; Antonini, Giovanni; Di Pasquale, Antonella; Garibaldi, Matteo; Morino, Stefania; Troili, Fernanda; Fionda, Laura; Di Pasquale, Antonella; Evoli, Amelia; Emilio Alboini, Paolo; D'amato, Valentina; Iorio, Raffaele; Inghilleri, Maurizio; Fionda, Laura; Frasca, Vittorio; Giacomelli, Elena; Gori, Maria Cristina; Lopergolo, Diego; Onesti, Emanuela; Frasca, Vittorio; Gabriele, Maria; Saccà, Francesco; Filla, Alessandro; Costabile, Teresa; Marano, Enrico; Fasanaro, Angiola; Marsili, Angela; Puorro, Giorgia; Antozzi, Carlo; Bonanno, Silvia; Camera, Giorgia; Locatelli, Alberta; Maggi, Lorenzo; Pasanisi, Maria; Campanella, Angela; Uzawa, Akiyuki; Kanai, Tetsuya; Kawaguchi, Naoki; Mori, Masahiro; Kaneko, Yoko; Kanzaki, Akiko; Kobayashi, Eri; Murai, Hiroyuki; Masaki, Katsuhisa; Matsuse, Dai; Matsushita, Takuya; Uehara, Taira; Shimpo, Misa; Jingu, Maki; Kikutake, Keiko; Nakamura, Yumiko; Sano, Yoshiko; Utsugisawa, Kimiaki; Nagane, Yuriko; Kamegamori, Ikuko; Tsuda, Tomoko; Fujii, Yuko; Futono, Kazumi; Ozawa, Yukiko; Mizugami, Aya; Saito, Yuka; Samukawa, Makoto; Suzuki, Hidekazu; Morikawa, Miyuki; Kamakura, Sachiko; Miyawaki, Eriko; Okumura, Meinoshin; Funaka, Soichiro; Kawamura, Tomohiro; Nakamori, Masayuki; Takahashi, Masanori; Taichi, Namie; Hasuike, Tomoya; Higuchi, Eriko; Kobayashi, Hisako; Osakada, Kaori; Shiraishi, Hirokazu; Miyazaki, Teiichiro; Motomura, Masakatsu; Mukaino, Akihiro; - 01a Articolo in rivista
rivista: NEUROLOGY (Wolters Kluwer Hagerstown MD: Lippincott Williams & Wilkins) pp. e610-e618 - issn: 1526-632X - wos: WOS:000657546900024 (30) - scopus: 2-s2.0-85100445590 (39)

11573/1603296 - 2021 - Eculizumab in refractory generalized myasthenia gravis previously treated with rituximab: subgroup analysis of REGAIN and its extension study
Siddiqi, Z. A.; Nowak, R. J.; Mozaffar, T.; O'brien, F.; Yountz, M.; Patti, F.; Mazia, C. G.; Wilken, M.; Wilken, M.; Barroso, F.; Saba, J.; Rugiero, M.; Bettini, M.; Chaves, M.; Vidal, G.; Garcia, A. D.; De Bleecker, J.; Van Den Abeele, G.; De Koning, K.; De Mey, K.; Mercelis, R.; Mahieu, D.; Wagemaekers, L.; Van Damme, P.; Depreitere, A.; Schotte, C.; Smetcoren, C.; Stevens, O.; Van Daele, S.; Vandenbussche, N.; Vanhee, A.; Verjans, S.; Vynckier, J.; D'hont, A.; Tilkin, P.; De Siqueira Carvalho, A. A.; Brockhausen, I. D.; Feder, D.; Ambrosio, D.; Cesar, P.; Melo, A. P.; Ribeiro, R. M.; Rocha, R.; Rosa, B. B.; Veiga, T.; Da Silva, L. A.; Engel, M. S.; Geraldo, J. G.; Da Penha Ananias Morita, M.; Coelho, E. N.; Paiva, G.; Pozo, M.; Prando, N.; Torres, D. D. M.; Butinhao, C. F.; Duran, G.; Fialho, T. A. S.; Da Silva, T. C. G.; Goncalves, L. O. M.; Pazetto, L. E.; Volpe, L. R. C.; Duca, L. S.; Friedrich, M. A. G.; Guerreiro, A.; Mohr, H.; Martins, M. P.; Da Cruz Pacheco, D.; Ferreira, L.; Macagnan, A. P.; Pinto, G.; De Cassia Santos, A.; Oliveira, A. S. B.; De Andrade, A. C. A.; Annes, M.; Silva, L. D.; Lino, V. C.; Pinto, W.; Assis, N.; Carrara, F.; Miranda, C.; Souza, I.; Fernandes, P.; Phan, C.; Narayan, J.; Blackmore, D.; Mallon, A.; Roderus, R.; Watt, E.; Vohanka, S.; Bednarik, J.; Chmelikova, M.; Cierny, M.; Toncrova, S.; Junkerova, J.; Kurkova, B.; Reguliova, K.; Zapletalova, O.; Pitha, J.; Novakova, I.; Tyblova, M.; Jurajdova, I.; Wolfova, M.; Andersen, H.; Harbo, T.; Vinge, L.; Krogh, S.; Mogensen, A.; Vissing, J.; Hojgaard, J.; Witting, N.; Autzen, A. M. O.; Pedersen, J.; Eralinna, J. -P.; Laaksonen, M.; Oksaranta, O.; Harrison, T.; Eriksson, J.; Rozsa, C.; Horvath, M.; Lovas, G.; Matolcsi, J.; Szabo, G.; Jakab, G.; Szabadosne, B.; Vecsei, L.; Dezsi, L.; Varga, E.; Konyane, M.; Antonini, G.; Di Pasquale, A.; Garibaldi, M.; Morino, S.; Troili, F.; Fionda, L.; Di Pasquale, A.; Garibaldi, M.; Sacca, F.; Filla, A.; Costabile, T.; Marano, E.; Fasanaro, A.; Marsili, A.; Puorro, G.; Mantegazza, R.; Antozzi, C.; Bonanno, S.; Camera, G.; Locatelli, A.; Maggi, L.; Pasanisi, M.; Campanella, A.; Evoli, A.; Alboini, P. E.; D'amato, V.; Iorio, R.; Inghilleri, M.; Fionda, L.; Frasca, V.; Giacomelli, E.; Gori, M.; Lopergolo, D.; Onesti, E.; Frasca, V.; Gabriele, M.; Uzawa, A.; Kanai, T.; Kawaguchi, N.; Mori, M.; Kaneko, Y.; Kanzaki, A.; Kobayashi, E.; Murai, H.; Masaki, K.; Matsuse, D.; Matsushita, T.; Uehara, T.; Shimpo, M.; Jingu, M.; Kikutake, K.; Nakamura, Y.; Sano, Y.; Utsugisawa, K.; Nagane, Y.; Kamegamori, I.; Tsuda, T.; Fujii, Y.; Futono, K.; Ozawa, Y.; Mizugami, A.; Saito, Y.; Samukawa, M.; Suzuki, H.; Morikawa, M.; Kamakura, S.; Miyawaki, E.; Shiraishi, H.; Miyazaki, T.; Motomura, M.; Mukaino, A.; Yoshimura, S.; Asada, S.; Yoshida, S.; Amamoto, S.; Kobashikawa, T.; Koga, M.; Maeda, Y.; Takada, K.; Takada, M.; Tsurumaru, M.; Yamashita, Y.; Yoshida, S.; Suzuki, Y.; Akiyama, T.; Narikawa, K.; Tano, O.; Tsukita, K.; Kurihara, R.; Meguro, F.; Fukuda, Y.; Sato, M.; Okumura, M.; Funaka, S.; Kawamura, T.; Nakamori, M.; Takahashi, M.; Taichi, N.; Hasuike, T.; Higuchi, E.; Kobayashi, H.; Osakada, K.; Imai, T.; Tsuda, E.; Shimohama, S.; Hayashi, T.; Hisahara, S.; Imai, T.; Kawamata, J.; Murahara, T.; Saitoh, M.; Shimohama, S.; Suzuki, S.; Yamamoto, D.; Ishiyama, Y.; Ishiyama, N.; Noshiro, M.; Takeyama, R.; Uwasa, K.; Yasuda, I.; Kim, B. -J.; Lee, C. N.; Koo, Y. S.; Seok, H. Y.; Kang, H. N.; Ra, H. J.; Kim, B. J.; Cho, E. B.; Choi, M. S.; Lee, H. L.; Min, J. -H.; Seok, J.; Lee, J. E.; Koh, D. Y.; Kwon, J. Y.; Park, S. A.; Choi, E. H.; Hong, Y. -H.; Ahn, S. -H.; Koo, D. L.; Lim, J. -S.; Shin, C. W.; Hwang, J. Y.; Kim, M.; Kim, S. M.; Jeong, H. -N.; Jung, J. W.; Kim, Y. -H.; Lee, H. S.; Shin, H. Y.; Hwang, E. B.; Shin, M.; Van Der Kooi, A.; De Visser, M.; Gibson, T.; Casasnovas, C.; Aguilo, M. A. A.; Homedes-Pedret, C.; Palacios, N. J.; Porras, L. D.; Santamaria, V. V.; Lazaro, A.; Tejedor, E. D.; Salcedo, P. G.; Fernandez-Fournier, M.; R - 01a Articolo in rivista
rivista: MUSCLE & NERVE (John Wiley & Sons Incorporated:Customer Service, 111 River Street:Hoboken, NJ 07030:(800)225-5945, (201)748-6000, EMAIL: societyinfo@wiley.com, INTERNET: http://www.wiley.com, Fax: (212)748-6551) pp. 662-669 - issn: 0148-639X - wos: WOS:000706979400001 (7) - scopus: 2-s2.0-85117104099 (7)

11573/1402033 - 2020 - Minimal Symptom Expression' in Patients With Acetylcholine Receptor Antibody-Positive Refractory Generalized Myasthenia Gravis Treated With Eculizumab
Gabriel Mazia, Claudio; Wilken, Miguel; Barroso, Fabio; Saba, Juliet; Rugiero, Marcelo; Bettini, Mariela; Chaves, Marcelo; Vidal, Gonzalo; Dalila Garcia, Alejandra; De Bleecker, Jan; Van Den Abeele, Guy; De Koning, Kathy; De Mey, Katrien; Mercelis, Rudy; Mahieu, Délphine; Wagemaekers, Linda; Van Damme, Philip; Depreitere, Annelies; Schotte, Caroline; Smetcoren, Charlotte; Stevens, Olivier; Van Daele, Sien; Vandenbussche, Nicolas; Vanhee, Annelies; Verjans, Sarah; Vynckier, Jan; D'hont, Ann; Tilkin, Petra; Alves De Siqueira Carvalho, Alzira; Dias Brockhausen, Igor; Feder, David; Ambrosio, Daniel; César, Pamela; Paula Melo, Ana; Martins Ribeiro, Renata; Rocha, Rosana; Bezerra Rosa, Bruno; Veiga, Thabata; Augusto Da Silva, Luiz; Santos Engel, Murilo; Gonçalves Geraldo, Jordana; Da Penha Ananias Morita, Maria; Nogueira Coelho, Erica; Paiva, Gabriel; Pozo, Marina; Prando, Natalia; Dada Martineli Torres, Debora; Fernanda Butinhao, Cristiani; Duran, Gustavo; Augusto Suriane Fialho, Tomás; Cristina Gomes Da Silva, Tamires; Otavio Maia Gonçalves, Luiz; Eduardo Pazetto, Lucas; Renata Cubas Volpe, Luciana; Souza Duca, Luciana; André Gheller Friedrich, Maurício; Guerreiro, Alexandre; Mohr, Henrique; Pereira Martins, Maurer; Da Cruz Pacheco, Daiane; Ferreira, Luciana; Paula Macagnan, Ana; Pinto, Graziela; De Cassia Santos, Aline; Souza Bulle Oliveira, Acary; Carolina Amaral De Andrade, Ana; Annes, Marcelo; Duarte Silva, Liene; Cavalcante Lino, Valeria; Pinto, Wladimir; Assis, Natália; Carrara, Fernanda; Miranda, Carolina; Souza, Iandra; Fernandes, Patrícia; Siddiqi, Zaeem; Phan, Cecile; Narayan, Jeffrey; Blackmore, Derrick; Mallon, Ashley; Roderus, Rikki; Watt, Elizabeth; Vohanka, Stanislav; Bednarik, Josef; Chmelikova, Magda; Cierny, Marek; Toncrova, Stanislava; Junkerova Barbora Kurkova, Jana; Reguliova, Katarina; Zapletalova, Olga; Pitha, Jiri; Novakova, Iveta; Tyblova, Michaela; Jurajdova, Ivana; Wolfova, Marcela; Andersen, Henning; Harbo, Thomas; Vinge, Lotte; Krogh, Susanne; Mogensen, Anita; Vissing, John; Højgaard, Joan; Witting, Nanna; Mette Ostergaard Autzen, Anne; Pedersen, Jane; Erälinna, Juha-Pekka; Laaksonen, Mikko; Oksaranta, Olli; Harrison, Tuula; Eriksson, Jaana; Rozsa, Csilla; Horvath, Melinda; Lovas, Gabor; Matolcsi, Judit; Szabo, Gyorgyi; Jakab, Gedeonne; Szabadosne, Brigitta; Vecsei, Laszlo; Dezsi, Livia; Varga, Edina; Konyane, Monika; Antonini, Giovanni; Di Pasquale, Antonella; Garibaldi, Matteo; Morino, Stefania; Troili, Fernanda; Fionda, Laura; Saccà, Francesco; Previous, ; Filla, Alessandro; Sub-Investigators, ; Costabile, Teresa; Marano, Enrico; Fasanaro, Angiola; Marsili, Angela; Puorro, Giorgia; Mantegazza, Renato; Antozzi, Carlo; Bonanno, Silvia; Camera, Giorgia; Locatelli, Alberta; Maggi, Lorenzo; Pasanisi, Maria; Campanella, Angela; Evoli, Amelia; Emilio Alboini, Paolo; D'amato, Valentina; Iorio, Raffaele; Inghilleri, Maurizio; Fionda, Laura; Frasca, Vittorio; Giacomelli, Elena; Gori, Maria Cristina; Lopergolo, Diego; Onesti, Emanuela; Frasca, Vittorio; Gabriele, Maria; Uzawa, Akiyuki; Kanai, Tetsuya; Kawaguchi, Naoki; Mori, Masahiro; Kaneko, Yoko; Kanzaki, Akiko; Kobayashi, Eri; Murai, Hiroyuki; Masaki, Katsuhisa; Matsuse, Dai; Matsushita, Takuya; Uehara, Taira; Shimpo, Misa; Jingu, Maki; Kikutake, Keiko; Nakamura, Yumiko; Sano, Yoshiko; Utsugisawa, Kimiaki; Nagane, Yuriko; Kamegamori, Ikuko; Tsuda, Tomoko; Fujii, Yuko; Futono, Kazumi; Ozawa, Yukiko; Mizugami, Aya; Saito, Yuka; Samukawa, Makoto; Suzuki, Hidekazu; Morikawa, Miyuki; Kamakura, Sachiko; Miyawaki, Eriko; Shiraishi, Hirokazu; Mitazaki, Teiichiro; Motomura, Masakatsu; Mukaino, Akihiro; Yoshimura, Shunsuke; Asada, Shizuka; Yoshida, Seiko; Amamoto, Shoko; Kobashikawa, Tomomi; Koga, Megumi; Maeda, Yasuko; Takada, Kazumi; Takada, Mihoko; Tsurumaru, Masako; Yamashita, Yumi; Yoshida, Seiko; Suzuki, Yasushi; Akiyama, Tetsuya; Narikawa, Koichi; Tano, Ohito; Tsukita, Kenichi; Kurihara, Rikako; Meguro, Fumie; - 01a Articolo in rivista
rivista: JOURNAL OF NEUROLOGY (Springer Verlag Germany:Tiergartenstrasse 17, D 69121 Heidelberg Germany:011 49 6221 3450, EMAIL: g.braun@springer.de, INTERNET: http://www.springer.de, Fax: 011 49 6221 345229) pp. - - issn: 0340-5354 - wos: WOS:000549382300001 (26) - scopus: 2-s2.0-85085089028 (29)

11573/1477816 - 2020 - Novel ACTA1 mutation causes late-presenting nemaline myopathy with unusual dark cores
Garibaldi, M.; Fattori, F.; Pennisi, E. M.; Merlonghi, G.; Fionda, L.; Vanoli, F.; Leonardi, L.; Bucci, E.; Morino, S.; Micaloni, A.; Tartaglione, T.; Uijterwijk, B.; Zierikzee, M.; Ottenheijm, C.; Bertini, E. S.; Stoppacciaro, A.; Raffa, S.; Salvetti, M.; Antonini, G. - 01a Articolo in rivista
rivista: NEUROMUSCULAR DISORDERS (Elsevier Science Limited:Oxford Fulfillment Center, PO Box 800, Kidlington Oxford OX5 1DX United Kingdom:011 44 1865 843000, 011 44 1865 843699, EMAIL: asianfo@elsevier.com, tcb@elsevier.co.UK, INTERNET: http://www.elsevier.com, http://www.elsevier.com/locate/shpsa/, Fax: 011 44 1865 843010) pp. - - issn: 0960-8966 - wos: (0) - scopus: 2-s2.0-85098620572 (3)

11573/1396999 - 2020 - Muscle involvement in myasthenia gravis: Expanding the clinical spectrum of Myasthenia-Myositis association from a large cohort of patients
Garibaldi, M.; Fionda, L.; Vanoli, F.; Leonardi, L.; Loreti, S.; Bucci, E.; Di Pasquale, A.; Morino, S.; Vizzaccaro, E.; Merlonghi, G.; Ceccanti, M.; Lucchini, M.; Mirabella, M.; Andreetta, F.; Pennisi, E. M.; Petrucci, A.; Salvetti, M.; Antonini, G. - 01g Articolo di rassegna (Review)
rivista: AUTOIMMUNITY REVIEWS (Amsterdam; London; New York; Oxford; Paris; Shannon; Tokyo: Elsevier Oxford: Elsevier Science) pp. 102498- - issn: 1568-9972 - wos: WOS:000527330700012 (24) - scopus: 2-s2.0-85081220949 (31)

11573/1477820 - 2020 - Gender effect on cardiac involvement in myotonic dystrophy type 1
Garibaldi, M.; Lauletta, A.; Bucci, E.; Fionda, L.; Vanoli, F.; Leonardi, L.; Alfieri, G.; Tufano, L.; Morino, S.; Merlonghi, G.; Anibaldi, P.; Salvetti, M.; Testa, M.; Antonini, G. - 01a Articolo in rivista
rivista: EUROPEAN JOURNAL OF NEUROLOGY (Lippincott, Williams & Wilkins:530 Walnut Street:Philadelphia, PA 19106:(800)638-3030, (301)223-2300, EMAIL: orders@lww.com, INTERNET: http://www.lww.com, Fax: (301)223-2320, (301)223-2320) pp. - - issn: 1351-5101 - wos: WOS:000601785400001 (4) - scopus: 2-s2.0-85098059659 (3)

11573/1439827 - 2020 - Nerve ultrasonography findings as possible pitfall in differential diagnosis between hereditary transthyretin amyloidosis with polyneuropathy and chronic inflammatory demyelinating polyneuropathy
Leonardi, Luca; Vanoli, Fiammetta; Fionda, Laura; Loreti, Simona; Garibaldi, Matteo; Morino, Stefania; Salvetti, Marco; Russo, Domitilla; Musumeci, Beatrice; Antonini, Giovanni - 01a Articolo in rivista
rivista: NEUROLOGICAL SCIENCES (Springer-Verlag Italia Srl:via Decembrio 28, 20137 Milan Italy:011 39 2 5425971, EMAIL: riccardi@springer.it, Fax: 011 39 2 55193360) pp. 1-4 - issn: 1590-3478 - wos: WOS:000571185200001 (8) - scopus: 2-s2.0-85091104497 (8)

11573/1433726 - 2020 - Consistent improvement with eculizumab across muscle groups in myasthenia gravis
Mantegazza, R.; O'brien, F. L.; Yountz, M.; Howard, J. F.; Gabriel Mazia, C.; Wilken, M.; Barroso, F.; Saba, J.; Rugiero, M.; Bettini, M.; Chaves, M.; Vidal, G.; Dalila Garcia, A.; De Bleecker, J.; Van Den Abeele, G.; De Koning, K.; De Mey, K.; Mercelis, R.; Mahieu, D.; Wagemaekers, L.; Van Damme, P.; Depreitere, A.; Schotte, C.; Smetcoren, C.; Stevens, O.; Van Daele, S.; Vandenbussche, N.; Vanhee, A.; Verjans, S.; Vynckier, J.; D'hont, A.; Tilkin, P.; Alves De Siqueira Carvalho, A.; Dias Brockhausen, I.; Feder, D.; Ambrosio, D.; Cesar, P.; Paula Melo, A.; Martins Ribeiro, R.; Rocha, R.; Bezerra Rosa, B.; Veiga, T.; Augusto Da Silva, L.; Santos Engel, M.; Goncalves Geraldo, J.; Da Penha Ananias Morita, M.; Nogueira Coelho, E.; Paiva, G.; Pozo, M.; Prando, N.; Torres, D. D. M.; Fernanda Butinhao, C.; Duran, G.; Augusto Suriane Fialho, T.; Gomes Da Silva, T. C.; Goncalves, L. O. M.; Eduardo Pazetto, L.; Renata Cubas Volpe, L.; Souza Duca, L.; Friedrich, M. A. G.; Guerreiro, A.; Mohr, H.; Pereira Martins, M.; Da Cruz Pacheco, D.; Ferreira, L.; Paula Macagnan, A.; Pinto, G.; De Cassia Santos, A.; Souza Bulle Oliveira, A.; Amaral De Andrade, A. C.; Annes, M.; Duarte Silva, L.; Cavalcante Lino, V.; Pinto, W.; Assis, N.; Carrara, F.; Miranda, C.; Souza, I.; Fernandes, P.; Siddiqi, Z.; Phan, C.; Narayan, J.; Blackmore, D.; Mallon, A.; Roderus, R.; Watt, E.; Vohanka, S.; Bednarik, J.; Chmelikova, M.; Cierny, M.; Toncrova, S.; Junkerova, J.; Kurkova, B.; Reguliova, K.; Zapletalova, O.; Pitha, J.; Novakova, I.; Tyblova, M.; Jurajdova, I.; Wolfova, M.; Andersen, H.; Harbo, T.; Vinge, L.; Krogh, S.; Mogensen, A.; Vissing, J.; Hojgaard, J.; Witting, N.; Mette Ostergaard Autzen, A.; Pedersen, J.; Eralinna, J. -P.; Laaksonen, M.; Oksaranta, O.; Harrison, T.; Eriksson, J.; Rozsa, C.; Horvath, M.; Lovas, G.; Matolcsi, J.; Szabo, G.; Jakab, G.; Szabadosne, B.; Vecsei, L.; Dezsi, L.; Varga, E.; Konyane, M.; Antonini, G.; Di Pasquale, A.; Garibaldi, M.; Morino, S.; Troili, F.; Fionda, L.; Pasquale, A.; Evoli, A.; Emilio Alboini, P.; D'amato, V.; Iorio, R.; Inghilleri, M.; Fionda, L.; Frasca, V.; Giacomelli, E.; Gori, M.; Lopergolo, D.; Onesti, E.; Frasca, V.; Gabriele, M.; Sacca, F.; Filla, A.; Costabile, T.; Marano, E.; Fasanaro, A.; Marsili, A.; Puorro, G.; Antozzi, C.; Bonanno, S.; Camera, G.; Locatelli, A.; Maggi, L.; Pasanisi, M.; Campanella, A.; Uzawa, A.; Kanai, T.; Kawaguchi, N.; Mori, M.; Kaneko, Y.; Kanzaki, A.; Kobayashi, E.; Murai, H.; Masaki, K.; Matsuse, D.; Matsushita, T.; Uehara, T.; Shimpo, M.; Jingu, M.; Kikutake, K.; Nakamura, Y.; Sano, Y.; Utsugisawa, K.; Nagane, Y.; Kamegamori, I.; Tsuda, T.; Fujii, Y.; Futono, K.; Ozawa, Y.; Mizugami, A.; Saito, Y.; Samukawa, M.; Suzuki, H.; Morikawa, M.; Kamakura, S.; Miyawaki, E.; Okumura, M.; Funaka, S.; Kawamura, T.; Nakamori, M.; Takahashi, M.; Taichi, N.; Hasuike, T.; Higuchi, E.; Kobayashi, H.; Osakada, K.; Shiraishi, H.; Miyazaki, T.; Motomura, M.; Mukaino, A.; Yoshimura, S.; Asada, S.; Yoshida, S.; Amamoto, S.; Kobashikawa, T.; Koga, M.; Maeda, Y.; Takada, K.; Takada, M.; Tsurumaru, M.; Yamashita, Y.; Suzuki, Y.; Akiyama, T.; Narikawa, K.; Tano, O.; Tsukita, K.; Kurihara, R.; Meguro, F.; Fukuda, Y.; Sato, M.; Imai, T.; Tsuda, E.; Shimohama, S.; Hayashi, T.; Hisahara, S.; Imai, T.; Kawamata, J.; Murahara, T.; Saitoh, M.; Shimohama, S.; Suzuki, S.; Yamamoto, D.; Ishiyama, Y.; Ishiyama, N.; Noshiro, M.; Takeyama, R.; Uwasa, K.; Yasuda, I.; Van Der Kooi, A.; De Visser, M.; Gibson, T.; Kim, B. -J.; Nyoung Lee, C.; Seo Koo, Y.; Youl Seok, H.; Nam Kang, H.; Ra, H.; Joon Kim, B.; Bin Cho, E.; Choi, M.; Lee, H.; Min, J. -H.; Seok, J.; Lee, J.; Koh, D. Y.; Kwon, J.; Park, S.; Haw Choi, E.; Hong, Y. -H.; Ahn, S. -H.; Lim Koo, D.; Lim, J. -S.; Won Shin, C.; Ye Hwang, J.; Kim, M.; Min Kim, S.; Jeong, H. -N.; Jung, J.; Kim, Y. -H.; Seok Lee, H.; Young Shin, H.; Bi Hwang, E.; Shin, M.; Casasnovas, C.; Antonia Alberti Aguilo, M.; Homedes-Pedret, C.; Julia Palacios, N.; Diez Porras, L.; Velez Santama - 01a Articolo in rivista
rivista: ANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY () pp. 1-13 - issn: 2328-9503 - wos: WOS:000551086500001 (12) - scopus: 2-s2.0-85088297453 (12)

11573/1348435 - 2019 - Eculizumab improves fatigue in refractory generalized myasthenia gravis
Andersen, H.; Mantegazza, R.; Wang, J. J.; O'brien, F.; Patra, K.; Howard, J. F.; Mazia, C. G.; Wilken, M.; Barroso, F.; Saba, J.; Rugiero, M.; Bettini, M.; Chaves, M.; Vidal, G.; Garcia, A. D.; Debleecker, J.; Van Denabeele, G.; Dekoning, K.; Demey, K.; Mercelis, R.; Mahieu, D.; Wagemaekers, L.; Vandamme, P.; Depreitere, A.; Schotte, C.; Smetcoren, C.; Stevens, O.; Vandaele, S.; Vandenbussche, N.; Vanhee, A.; Verjans, S.; Vynckier, J.; D'hondt, A.; Tilkin, P.; Alvesdesiqueira Carvalho, A.; Diasbrockhausen, I.; Feder, D.; Ambrosio, D.; Cesar, P.; Melo, A. P.; Martinsribeiro, R.; Rocha, R.; Bezerrarosa, B.; Veiga, T.; Dasilva, L. A.; Santosengel, M.; Goncalvesgeraldo, J.; Dapenha Ananiasmorita, M.; Nogueiracoelho, E.; Paiva, G.; Pozo, M.; Prando, N.; Martinelitorres, D. D.; Butinhao, C. F.; Duran, G.; Gomes Dasilva, T. C.; Otavio Maiagoncalves, L.; Pazetto, L. E.; Fialho, T. A. S.; Renata Cubasvolpe, L.; Souzaduca, L.; Ghellerfriedrich, M. A.; Guerreiro, A.; Mohr, H.; Pereiramartins, M.; Dacruz Pacheco, D.; Ferreira, L.; Macagnan, A. P.; Pinto, G.; Decassia Santos, A.; Souza Bulleoliveira, A.; Amaralandrade, A. C.; Annes, M.; Duarte Silva, L.; Cavalcantelino, V.; Pinto, W.; Assis, N.; Carrara, F.; Miranda, C.; Souza, I.; Fernandes, P.; Siddiqi, Z.; Phan, C.; Narayan, J.; Blackmore, D.; Mallon, A.; Roderus, R.; Watt, E.; Vohanka, S.; Bednarik, J.; Chmelikova, M.; Cierny, M.; Toncrova, S.; Junkerova, J.; Kurkova, B.; Reguliova, K.; Zapletalova, O.; Pitha, J.; Novakova, I.; Tyblova, M.; Jurajdova, I.; Wolfova, M.; Harbo, T.; Vinge, L.; Krogh, S.; Mogensen, A.; Vissing, J.; Hojgaard, J.; Witting, N.; Ostergaardautzen, A.; Pedersen, J.; Eralinna, J. -P.; Laaksonen, M.; Oksaranta, O.; Harrison, T.; Eriksson, J.; Rozsa, C.; Horvath, M.; Lovas, G.; Matolcsi, J.; Szabo, G.; Jakab, G.; Szabadosne, B.; Vecsei, L.; Dezsi, L.; Varga, E.; Konyane, M.; Antonini, G.; Dipasquale, A.; Garibaldi, M.; Morino, S.; Troili, F.; Fionda, L.; Filla, A.; Costabile, T.; Marano, E.; Sacca, F.; Fasanaro, A.; Marsili, A.; Puorro, G.; Antozzi, C.; Bonanno, S.; Camera, G.; Locatelli, A.; Maggi, L.; Pasanisi, M.; Campanella, A.; Evoli, A.; Alboini, P. E.; D'amato, V.; Iorio, R.; Inghilleri, M.; Fionda, L.; Frasca, V.; Giacomelli, E.; Gori, M.; Lopergolo, D.; Onesti, E.; Frasca, V.; Gabriele, M.; Uzawa, A.; Kanai, T.; Kawaguchi, N.; Mori, M.; Kaneko, Y.; Kanzaki, A.; Kobayashi, E.; Murai, H.; Masaki, K.; Matsuse, D.; Matsushita, T.; Uehara, T.; Shimpo, M.; Jingu, M.; Kikutake, K.; Nakamura, Y.; Sano, Y.; Utsugisawa, K.; Nagane, Y.; Kamegamori, I.; Tsuda, T.; Fujii, Y.; Futono, K.; Ozawa, Y.; Mizugami, A.; Saito, Y.; Suzuki, H.; Morikawa, M.; Samukawa, M.; Kamakura, S.; Miyawaki, E.; Shiraishi, H.; Mitazaki, T.; Motomura, M.; Mukaino, A.; Yoshimura, S.; Asada, S.; Yoshida, S.; Amamoto, S.; Kobashikawa, T.; Koga, M.; Maeda, Y.; Takada, K.; Takada, M.; Tsurumaru, M.; Yamashita, Y.; Suzuki, Y.; Akiyama, T.; Narikawa, K.; Tano, O.; Tsukita, K.; Kurihara, R.; Meguro, F.; Fukuda, Y.; Sato, M.; Okumura, M.; Funaka, S.; Kawamura, T.; Makamori, M.; Takahashi, M.; Taichi, N.; Hasuike, T.; Higuchi, E.; Kobayashi, H.; Osakada, K.; Imai, T.; Tsuda, E.; Shimohama, S.; Hayashi, T.; Hisahara, S.; Kawamata, J.; Murahara, T.; Saitoh, M.; Suzuki, S.; Yamamoto, D.; Ishiyama, Y.; Ishiyama, N.; Noshiro, M.; Takeyama, R.; Uwasa, K.; Yasuda, I.; Van Derkooi, A.; Devisser, M.; Gibson, T.; Kim, B. -J.; Lee, C. N.; Koo, Y. S.; Seok, H. Y.; Kang, H. N.; Ra, H. J.; Kim, B. J.; Cho, E. B.; Choi, M. S.; Lee, H. L.; Min, J. -H.; Seok, J.; Lee, J. E.; Koh, D. Y.; Kwon, J. Y.; Park, S. A.; Choi, E. H.; Hong, Y. -H.; Ahn, S. -H.; Koo, D. L.; Lim, J. -S.; Shin, C. W.; Hwang, J. Y.; Kim, M.; Kim, S. M.; Jeong, H. -N.; Jung, J. W.; Kim, Y. -H.; Lee, H. S.; Shin, H. Y.; Hwang, E. B.; Shin, M.; Casasnovas, C.; Albertiaguilo, M. A.; Homedes-Pedret, C.; Juliapalacios, N.; Diezporras, L.; Velezsantamaria, V.; Lazaro, A.; Dieztejedor, E.; Gomez Salcedo, P.; Fernandez-Fournier, M.; Lopezruiz, P.; Rodriguez - 01a Articolo in rivista
rivista: QUALITY OF LIFE RESEARCH (Kluwer Academic Publishers:Journals Department, PO Box 322, 3300 AH Dordrecht Netherlands:011 31 78 6576050, EMAIL: frontoffice@wkap.nl, kluweronline@wkap.nl, INTERNET: http://www.kluwerlaw.com, Fax: 011 31 78 6576254) pp. 2247-2254 - issn: 0962-9343 - wos: WOS:000475577200021 (28) - scopus: 2-s2.0-85065135150 (33)

11573/1677302 - 2019 - Correction to: Eculizumab improves fatigue in refractory generalized myasthenia gravis (Quality of Life Research, (2019), 28, 8, (2247-2254), 10.1007/s11136-019-02148-2)
Andersen, H.; Mantegazza, R.; Wang, J. J.; O'brien, F.; Patra, K.; Howard, J. F.; Mazia, C. G.; Wilken, M.; Barroso, F.; Saba, J.; Rugiero, M.; Bettini, M.; Chaves, M.; Vidal, G.; Garcia, A. D.; Debleecker, J.; Van Denabeele, G.; Dekoning, K.; Demey, K.; Mercelis, R.; Mahieu, D.; Wagemaekers, L.; Vandamme, P.; Depreitere, A.; Schotte, C.; Smetcoren, C.; Stevens, O.; Vandaele, S.; Vandenbussche, N.; Vanhee, A.; Verjans, S.; Vynckier, J.; D'hondt, A.; Tilkin, P.; Alvesdesiqueira Carvalho, A.; Diasbrockhausen, I.; Feder, D.; Ambrosio, D.; Cesar, P.; Melo, A. P.; Martinsribeiro, R.; Rocha, R.; Bezerrarosa, B.; Veiga, T.; Dasilva, L. A.; Santosengel, M.; Goncalvesgeraldo, J.; Dapenha Ananiasmorita, M.; Nogueiracoelho, E.; Paiva, G.; Pozo, M.; Prando, N.; Martinelitorres, D. D.; Butinhao, C. F.; Duran, G.; Gomes Dasilva, T. C.; Otavio Maiagoncalves, L.; Pazetto, L. E.; Fialho, T. A. S.; Renata Cubasvolpe, L.; Souzaduca, L.; Ghellerfriedrich, M. A.; Guerreiro, A.; Mohr, H.; Pereiramartins, M.; Dacruz Pacheco, D.; Ferreira, L.; Macagnan, A. P.; Pinto, G.; Decassia Santos, A.; Souza Bulleoliveira, A.; Amaralandrade, A. C.; Annes, M.; Duarte Silva, L.; Cavalcantelino, V.; Pinto, W.; Assis, N.; Carrara, F.; Miranda, C.; Souza, I.; Fernandes, P.; Siddiqi, Z.; Phan, C.; Narayan, J.; Blackmore, D.; Mallon, A.; Roderus, R.; Watt, E.; Vohanka, S.; Bednarik, J.; Chmelikova, M.; Cierny, M.; Toncrova, S.; Junkerova, J.; Kurkova, B.; Reguliova, K.; Zapletalova, O.; Pitha, J.; Novakova, I.; Tyblova, M.; Jurajdova, I.; Wolfova, M.; Harbo, T.; Vinge, L.; Krogh, S.; Mogensen, A.; Vissing, J.; Hojgaard, J.; Witting, N.; Ostergaardautzen, A.; Pedersen, J.; Eralinna, J. -P.; Laaksonen, M.; Oksaranta, O.; Harrison, T.; Eriksson, J.; Rozsa, C.; Horvath, M.; Lovas, G.; Matolcsi, J.; Szabo, G.; Jakab, G.; Szabadosne, B.; Vecsei, L.; Dezsi, L.; Varga, E.; Konyane, M.; Antonini, G.; Dipasquale, A.; Garibaldi, M.; Morino, S.; Troili, F.; Fionda, L.; Filla, A.; Costabile, T.; Marano, E.; Sacca, F.; Fasanaro, A.; Marsili, A.; Puorro, G.; Antozzi, C.; Bonanno, S.; Camera, G.; Locatelli, A.; Maggi, L.; Pasanisi, M.; Campanella, A.; Evoli, A.; Alboini, P. E.; D'amato, V.; Iorio, R.; Inghilleri, M.; Fionda, L.; Frasca, V.; Giacomelli, E.; Gori, M.; Lopergolo, D.; Onesti, E.; Frasca, V.; Gabriele, M.; Uzawa, A.; Kanai, T.; Kawaguchi, N.; Mori, M.; Kaneko, Y.; Kanzaki, A.; Kobayashi, E.; Murai, H.; Masaki, K.; Matsuse, D.; Matsushita, T.; Uehara, T.; Shimpo, M.; Jingu, M.; Kikutake, K.; Nakamura, Y.; Sano, Y.; Utsugisawa, K.; Nagane, Y.; Kamegamori, I.; Tsuda, T.; Fujii, Y.; Futono, K.; Ozawa, Y.; Mizugami, A.; Saito, Y.; Suzuki, H.; Morikawa, M.; Samukawa, M.; Kamakura, S.; Miyawaki, E.; Shiraishi, H.; Mitazaki, T.; Motomura, M.; Mukaino, A.; Yoshimura, S.; Asada, S.; Yoshida, S.; Amamoto, S.; Kobashikawa, T.; Koga, M.; Maeda, Y.; Takada, K.; Takada, M.; Tsurumaru, M.; Yamashita, Y.; Suzuki, Y.; Akiyama, T.; Narikawa, K.; Tano, O.; Tsukita, K.; Kurihara, R.; Meguro, F.; Fukuda, Y.; Sato, M.; Okumura, M.; Funaka, S.; Kawamura, T.; Makamori, M.; Takahashi, M.; Taichi, N.; Hasuike, T.; Higuchi, E.; Kobayashi, H.; Osakada, K.; Imai, T.; Tsuda, E.; Shimohama, S.; Hayashi, T.; Hisahara, S.; Kawamata, J.; Murahara, T.; Saitoh, M.; Suzuki, S.; Yamamoto, D.; Ishiyama, Y.; Ishiyama, N.; Noshiro, M.; Takeyama, R.; Uwasa, K.; Yasuda, I.; Van Derkooi, A.; Devisser, M.; Gibson, T.; Kim, B. -J.; Lee, C. N.; Koo, Y. S.; Seok, H. Y.; Kang, H. N.; Ra, H. J.; Kim, B. J.; Cho, E. B.; Choi, M. S.; Lee, H. L.; Min, J. -H.; Seok, J.; Lee, J. E.; Koh, D. Y.; Kwon, J. Y.; Park, S. A.; Choi, E. H.; Hong, Y. -H.; Ahn, S. -H.; Koo, D. L.; Lim, J. -S.; Shin, C. W.; Hwang, J. Y.; Kim, M.; Kim, S. M.; Jeong, H. -N.; Jung, J. W.; Kim, Y. -H.; Lee, H. S.; Shin, H. Y.; Hwang, E. B.; Shin, M.; Casasnovas, C.; Albertiaguilo, M. A.; Homedes-Pedret, C.; Juliapalacios, N.; Diezporras, L.; Velezsantamaria, V.; Lazaro, A.; Dieztejedor, E.; Gomez Salcedo, P.; Fernandez-Fournier, M.; Lopezruiz, P.; Rodriguez - 01b Commento, Erratum, Replica e simili
rivista: QUALITY OF LIFE RESEARCH (Kluwer Academic Publishers:Journals Department, PO Box 322, 3300 AH Dordrecht Netherlands:011 31 78 6576050, EMAIL: frontoffice@wkap.nl, kluweronline@wkap.nl, INTERNET: http://www.kluwerlaw.com, Fax: 011 31 78 6576254) pp. 2255- - issn: 0962-9343 - wos: WOS:000475577200022 (0) - scopus: 2-s2.0-85066885728 (0)

11573/1219606 - 2019 - Nerve high resolution ultrasonography in Tangier disease
Di Pasquale, A; Leonardi, L; Fionda, L; Vanoli, F; Garibaldi, M; Inghilleri, M; Ceccanti, M; Cambieri, C; Onesti, E; Antonini, G - 01a Articolo in rivista
rivista: MUSCLE & NERVE (John Wiley & Sons Incorporated:Customer Service, 111 River Street:Hoboken, NJ 07030:(800)225-5945, (201)748-6000, EMAIL: societyinfo@wiley.com, INTERNET: http://www.wiley.com, Fax: (212)748-6551) pp. 1-4 - issn: 0148-639X - wos: WOS:000466448800018 (2) - scopus: 2-s2.0-85061275196 (2)

11573/1316574 - 2019 - Nerve high-resolution ultrasonography in peripheral nerve injuries associated with supracondylar humeral fractures in children
Leonardi, L.; Loreti, S.; Di Pasquale, A.; Morino, S.; Fionda, L.; Vanoli, F.; Garibaldi, M.; Antonini, G. - 01a Articolo in rivista
rivista: JOURNAL OF CLINICAL NEUROSCIENCE (Amsterdam: Elsevier Science Ltd. South Melbourne Vic.: Churchill Livingstone Harcourt Publishers Limited) pp. 1339- - issn: 0967-5868 - wos: WOS:000515444800021 (1) - scopus: 2-s2.0-85071652579 (1)

11573/1348469 - 2019 - Long-term safety and efficacy of eculizumab in generalized myasthenia gravis
Muppidi, S.; Utsugisawa, K.; Benatar, M.; Murai, H.; Barohn, R. J.; Illa, I.; Jacob, S.; Vissing, J.; Burns, T. M.; Kissel, J. T.; Nowak, R. J.; Andersen, H.; Casasnovas, C.; De Bleecker, J. L.; Vu, T. H.; Mantegazza, R.; O'brien, F. L.; Wang, J. J.; Fujita, K. P.; Howard, J. F.; Mazia, C. G.; Wilken, M.; Barroso, F.; Saba, J.; Rugiero, M.; Bettini, M.; Chaves, M.; Vidal, G.; Garcia, A. D.; Van Den Abeele, G.; De Koning, K.; De Mey, K.; Mercelis, R.; Mahieu, D.; Wagemaekers, L.; Van Damme, P.; Depreitere, A.; Schotte, C.; Smetcoren, C.; Stevens, O.; Van Daele, S.; Vandenbussche, N.; Vanhee, A.; Verjans, S.; Vynckier, J.; D'hondt, A.; Tilkin, P.; Alves De Siqueira Carvalho, A.; Dias Brockhausen, I.; Feder, D.; Ambrosio, D.; Cesar, P.; Melo, A. P.; Martins Ribeiro, R.; Rocha, R.; Bezerra Rosa, B.; Veiga, T.; Da Silva, L. A.; Santos Engel, M.; Goncalves Geraldo, J.; Ananias Morita, M. D. P.; Nogueira Coelho, E.; Paiva, G.; Pozo, M.; Prando, N.; Martineli Torres, D. D.; Butinhao, C. F.; Duran, G.; Gomes Da Silva, T. C.; Otavio Maia Goncalves, L.; Pazetto, L. E.; Fialho, T. A. S.; Renata Cubas Volpe, L.; Souza Duca, L.; Gheller Friedrich, M. A.; Guerreiro, A.; Mohr, H.; Pereira Martins, M.; Da Cruz Pacheco, D.; Ferreira, L.; Macagnan, A. P.; Pinto, G.; De Cassia Santos, A.; Souza Bulle Oliveira, A.; Amaral Andrade, A. C.; Annes, M.; Duarte Silva, L.; Cavalcante Lino, V.; Pinto, W.; Assis, N.; Carrara, F.; Miranda, C.; Souza, I.; Fernandes, P.; Siddiqi, Z.; Phan, C.; Narayan, J.; Blackmore, D.; Mallon, A.; Roderus, R.; Watt, E.; Vohanka, S.; Bednarik, J.; Chmelikova, M.; Cierny, M.; Toncrova, S.; Junkerova, J.; Kurkova, B.; Reguliova, K.; Zapletalova, O.; Pitha, J.; Novakova, I.; Tyblova, M.; Jurajdova, I.; Wolfova, M.; Harbo, T.; Vinge, L.; Krogh, S.; Mogensen, A.; Hojgaard, J.; Witting, N.; Ostergaard Autzen, A.; Pedersen, J.; Eralinna, J. -P.; Laaksonen, M.; Oksaranta, O.; Harrison, T.; Eriksson, J.; Rozsa, C.; Horvath, M.; Lovas, G.; Matolcsi, J.; Szabo, G.; Jakab, G.; Szabadosne, B.; Vecsei, L.; Dezsi, L.; Varga, E.; Konyane, M.; Antonini, G.; Di Pasquale, A.; Garibaldi, M.; Morino, S.; Troili, F.; Fionda, L.; Filla, A.; Costabile, T.; Marano, E.; Sacca, F.; Fasanaro, A.; Marsili, A.; Puorro, G.; Antozzi, C.; Bonanno, S.; Camera, G.; Locatelli, A.; Maggi, L.; Pasanisi, M.; Campanella, A.; Evoli, A.; Alboini, P. E.; D'amato, V.; Iorio, R.; Inghilleri, M.; Fionda, L.; Frasca, V.; Giacomelli, E.; Gori, M.; Lopergolo, D.; Frasca, V.; Gabriele, M.; Uzawa, A.; Kanai, T.; Kawaguchi, N.; Mori, M.; Kaneko, Y.; Kanzaki, A.; Kobayashi, E.; Masaki, K.; Matsuse, D.; Matsushita, T.; Uehara, T.; Shimpo, M.; Jingu, M.; Kikutake, K.; Nakamura, Y.; Sano, Y.; Nagane, Y.; Kamegamori, I.; Tsuda, T.; Fujii, Y.; Futono, K.; Ozawa, Y.; Mizugami, A.; Saito, Y.; Suzuki, H.; Morikawa, M.; Samukawa, M.; Kamakura, S.; Miyawaki, E.; Shiraishi, H.; Mitazaki, T.; Motomura, M.; Mukaino, A.; Yoshimura, S.; Asada, S.; Yoshida, S.; Amamoto, S.; Kobashikawa, T.; Koga, M.; Maeda, Y.; Takada, K.; Takada, M.; Tsurumaru, M.; Yamashita, Y.; Suzuki, Y.; Akiyama, T.; Narikawa, K.; Tano, O.; Tsukita, K.; Kurihara, R.; Meguro, F.; Fukuda, Y.; Sato, M.; Okumura, M.; Funaka, S.; Kawamura, T.; Makamori, M.; Takahashi, M.; Taichi, N.; Hasuike, T.; Higuchi, E.; Kobayashi, H.; Osakada, K.; Imai, T.; Tsuda, E.; Shimohama, S.; Hayashi, T.; Hisahara, S.; Kawamata, J.; Murahara, T.; Saitoh, M.; Suzuki, S.; Yamamoto, D.; Ishiyama, Y.; Ishiyama, N.; Noshiro, M.; Takeyama, R.; Uwasa, K.; Yasuda, I.; Van Der Kooi, A.; De Visser, M.; Gibson, T.; Kim, B. -J.; Lee, C. N.; Koo, Y. S.; Seok, H. Y.; Kang, H. N.; Ra, H.; Kim, B. J.; Cho, E. B.; Choi, M.; Lee, H.; Min, J. -H.; Seok, J.; Lee, J.; Koh, D. Y.; Kwon, J.; Park, S.; Choi, E. H.; Hong, Y. -H.; Ahn, S. -H.; Koo, D. L.; Lim, J. -S.; Shin, C. W.; Hwang, J. Y.; Kim, M.; Kim, S. M.; Jeong, H. -N.; Jung, J.; Kim, Y. -H.; Lee, H. S.; Shin, H. Y.; Hwang, E. B.; Shin, M.; Alberti Aguilo, M. A.; Homedes-Pedret, C.; Julia Palacios, N.; Diez Porr - 01a Articolo in rivista
rivista: MUSCLE & NERVE (John Wiley & Sons Incorporated:Customer Service, 111 River Street:Hoboken, NJ 07030:(800)225-5945, (201)748-6000, EMAIL: societyinfo@wiley.com, INTERNET: http://www.wiley.com, Fax: (212)748-6551) pp. 14-24 - issn: 0148-639X - wos: WOS:000471831900011 (123) - scopus: 2-s2.0-85062729927 (152)

11573/1700722 - 2019 - Long-term efficacy and safety of eculizumab in Japanese patients with generalized myasthenia gravis. A subgroup analysis of the REGAIN open-label extension study
Murai, Hiroyuki; Uzawa, Akiyuki; Suzuki, Yasushi; Imai, Tomihiro; Shiraishi, Hirokazu; Suzuki, Hidekazu; Okumura, Meinoshin; O'brien, Fanny; Wang, Jing-Jing; Fujita, Kenji P; Kimiaki, Utsugisawa; Claudio Gabriel Mazia 11, ; Miguel Wilken 11, ; Fabio Barroso 11, ; Juliet Saba 11, ; Marcelo Rugiero 12, ; Mariela Bettini 12, ; Marcelo Chaves 12, ; Gonzalo Vidal 12, ; Alejandra Dalila Garcia 12, ; Jan De Bleecker 13, ; Guy Van Den Abeele 13, ; Kathy De Koning 13, ; Katrien De Mey 13, ; Rudy Mercelis 14, ; Délphine Mahieu 14, ; Linda Wagemaekers 14, ; Philip Van Damme 15, ; Annelies Depreitere 16, ; Caroline Schotte 16, ; Charlotte Smetcoren 16, ; Olivier Stevens 16, ; Sien Van Daele 16, ; Nicolas Vandenbussche 16, ; Annelies Vanhee 16, ; Sarah Verjans 16, ; Jan Vynckier 16, ; Ann D'hondt 16, ; Petra Tilkin 16, ; Alzira Alves De Siqueira Carvalho 17, ; Igor Dias Brockhausen 17, ; David Feder 17, ; Daniel Ambrosio 17, ; Pamela César 17, ; Ana Paula Melo 17, ; Renata Martins Ribeiro 17, ; Rosana Rocha 17, ; Bruno Bezerra Rosa 17, ; Thabata Veiga 17, ; Luiz Augusto Da Silva 17, ; Murilo Santos Engel 17, ; Jordana Gonçalves Geraldo 17, ; Maria Da Penha Ananias Morita 18, ; Erica Nogueira Coelho 18, ; Gabriel Paiva 18, ; Marina Pozo 18, ; Natalia Prando 18, ; Debora Dada Martineli Torres 18, ; Cristiani Fernanda Butinhao 18, ; Gustavo Duran 18, ; Tamires Cristina Gomes Da Silva 18, ; Luiz Otavio Maia Gonçalves 18, ; Lucas Eduardo Pazetto 18, ; Tomás Augusto Suriane Fialho 18, ; Luciana Renata Cubas Volpe 18, ; Luciana Souza Duca 18, ; Acary Souza Bulle Oliveira 19, ; Ana Carolina Amaral Andrade 19, ; Marcelo Annes 19, ; Liene Duarte Silva 19, ; Valeria Cavalcante Lino 19, ; Wladimir Pinto 19, ; Natália Assis 19, ; Fernanda Carrara 19, ; Carolina Miranda 19, ; Iandra Souza 19, ; Patricia Fernandes 19, ; Zaeem Siddiqi 20, ; Cecile Phan 20, ; Jeffrey Narayan 20, ; Derrick Blackmore 20, ; Ashley Mallon 20, ; Rikki Roderus 20, ; Elizabeth Watt 20, ; Jana Junkerova 21, ; Barbora Kurkova 21, ; Katarina Reguliova 21, ; Olga Zapletalova 21, ; Jiri Pitha 22, ; Iveta Novakova 22, ; Michaela Tyblova 22, ; Ivana Jurajdova 22, ; Marcela Wolfova 22, ; Henning Andersen 23, ; Thomas Harbo 23, ; Lotte Vinge 23, ; Susanne Krogh 23, ; Anita Mogensen 23, ; John Vissing 24, ; Joan Højgaard 24, ; Nanna Witting 24, ; Anne Mette Ostergaard Autzen 24, ; Jane Pedersen 24, ; Juha-Pekka Eralinna 25, ; Mikko Laaksonen 25, ; Olli Oksaranta 25, ; Tuula Harrison 25, ; Jaana Eriksson 25, ; Csilla Rozsa 26, ; Melinda Horvath 26, ; Gabor Lovas 26, ; Judit Matolcsi 26, ; Gyorgyi Szabo 26, ; Gedeonne Jakab 26, ; Brigitta Szabadosne 26, ; Antonini, Giovanni; Di Pasquale, Antonella; Garibaldi, Matteo; Morino, Stefania; Troili, Fernanda; Fionda, Laura; Allessandro Filla 28, ; Teresa Costabile 28, ; Enrico Marano 28, ; Francesco Saccà 28, ; Angiola Fasanaro 28, ; Angela Marsili 28, ; Giorgia Puorro 28, ; Renato Mantegazza 29, ; Carlo Antozzi 29, ; Silvia Bonanno 29, ; Giorgia Camera 29, ; Alberta Locatelli 29, ; Lorenzo Maggi 29, ; Maria Pasanisi 29, ; Angela Campanella 29, ; Amelia Evoli 30, ; Paolo Emilio Alboini 30, ; Valentina D'amato 30, ; Raffaele Iorio 30, ; Tetsuya Kanai 31, ; Naoki Kawaguchi 31, ; Masahiro Mori 31, ; Yoko Kaneko 31, ; Akiko Kanzaki 31, ; Eri Kobayashi 31, ; Katsuhisa Masaki 32, ; Dai Matsuse 32, ; Takuya Matsushita 32, ; Taira Uehara 32, ; Misa Shimpo 32, ; Maki Jingu 32, ; Keiko Kikutake 32, ; Yumiko Nakamura 32, ; Yoshiko Sano 32, ; Yuriko Nagane 33, ; Ikuko Kamegamori 33, ; Tomoko Tsuda 33, ; Yuko Fujii 33, ; Kazumi Futono 33, ; Yukiko Ozawa 33, ; Aya Mizugami 33, ; Yuka Saito 33, ; Miyuki Morikawa 34, ; Makoto Samukawa 34, ; Sachiko Kamakura 34, ; Eriko Miyawaki 34, ; Teiichiro Mitazaki 35, ; Masakatsu Motomura 35, ; Akihiro Mukaino 35, ; Shunsuke Yoshimura 35, ; Shizuka Asada 35, ; Seiko Yoshida 35, ; Shoko Amamoto 35, ; Tomomi Kobashikawa 35, ; Megumi Koga 35, ; Yasuko Maeda 35, ; Kazumi Takada 35 - 01a Articolo in rivista
rivista: JOURNAL OF THE NEUROLOGICAL SCIENCES (Elsevier BV:PO Box 211, 1000 AE Amsterdam Netherlands:011 31 20 4853757, 011 31 20 4853642, 011 31 20 4853641, EMAIL: nlinfo-f@elsevier.nl, INTERNET: http://www.elsevier.nl, Fax: 011 31 20 4853598) pp. 1-8 - issn: 0022-510X - wos: WOS:000503097600026 (11) - scopus: 2-s2.0-85074350335 (14)

11573/1123949 - 2018 - A 34-year longitudinal study on long-term cardiac outcomes in DM1 patients with normal ECG at baseline at an Italian clinical centre
Bucci, Elisabetta; Testa, Marco; Licchelli, Loretta; Frattari, Alessandra; El Halabieh, Nadia Attalla; Gabriele, Erica; Pignatelli, Giulia; De Santis, Tiziana; Fionda, Laura; Vanoli, Fiammetta; Morino, Stefania; Garibaldi, Matteo; Di Pasquale, Antonella; Vanacore, Nicola; Botta, Annalisa; Antonini, Giovanni - 01a Articolo in rivista
rivista: JOURNAL OF NEUROLOGY (Springer Verlag Germany:Tiergartenstrasse 17, D 69121 Heidelberg Germany:011 49 6221 3450, EMAIL: g.braun@springer.de, INTERNET: http://www.springer.de, Fax: 011 49 6221 345229) pp. 885-895 - issn: 0340-5354 - wos: WOS:000428928200017 (8) - scopus: 2-s2.0-85041930746 (11)

11573/1120950 - 2018 - Multifocal motor neuropathy following treatment with adalimumab for ulcerative colitis
Fionda, Laura; Vanoli, Fiammetta; Di Pasquale, Antonella; Leonardi, Luca; Morino, Stefania; Antonini, Giovanni - 01f Lettera, Nota
rivista: JOURNAL OF NEUROLOGY (Springer Verlag Germany:Tiergartenstrasse 17, D 69121 Heidelberg Germany:011 49 6221 3450, EMAIL: g.braun@springer.de, INTERNET: http://www.springer.de, Fax: 011 49 6221 345229) pp. 1466-1468 - issn: 0340-5354 - wos: WOS:000434462300027 (2) - scopus: 2-s2.0-85047134482 (2)

11573/1201162 - 2018 - Widening the phenotypical spectrum of EGR2-related CMT: unusual phenotype for R409W mutation
Leonardi, Luca; Garibaldi, Matteo; Fionda, Laura; Vanoli, Fiammetta; Loreti, Simona; Morino, Stefania; Antonini, Giovanni - 01a Articolo in rivista
rivista: CLINICAL NEUROPHYSIOLOGY (Elsevier Science Ireland Limited:PO Box 85, Limerick Ireland:011 353 61 709600, 011 353 61 61944, EMAIL: usinfo-f@elsevier.com, INTERNET: http://www.elsevier.com, Fax: 011 353 61 709114) pp. 93-94 - issn: 1388-2457 - wos: WOS:000454141500011 (3) - scopus: 2-s2.0-85057053333 (2)

11573/1127139 - 2017 - Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN). a phase 3, randomised, double-blind, placebo-controlled, multicentre study
Howard, James F; Utsugisawa, Kimiaki; Benatar, Michael; Murai, Hiroyuki; Barohn, Richard J; Illa, Isabel; Jacob, Saiju; Vissing, John; Burns, Ted M; Kissel, John T; Muppidi, Srikanth; Nowak, Richard J; O'brien, Fanny; Wang, Jing-Jing; Mantegazza, Renato; Mazia, Claudio Gabriel; Wilken, Miguel; Ortea, Carolina; Saba, Juliet; Rugiero, Marcelo; Bettini, Mariela; Vidal, Gonzalo; Garcia, Alejandra Dalila; Lamont, Phillipa; Leong, Wai-Kuen; Boterhoven, Heidi; Fyfe, Beverly; Roberts, Leslie; Jasinarachchi, Mahi; Willlems, Natasha; Wanschitz, Julia; Löscher, Wolfgang; De Bleecker, Jan; Van Den Abeele, Guy; De Koning, Kathy; De Mey, Katrien; Mercelis, Rudy; Wagemaekers, Linda; Mahieu, Delphine; Van Damme, Philip; Smetcoren, Charlotte; Stevens, Olivier; Verjans, Sarah; D'hondt, Ann; Tilkin, Petra; Alves De Siqueira Carvalho, Alzira; Hasan, Rosa; Dias Brockhausen, Igor; Feder, David; Ambrosio, Daniel; Melo, Ana Paula; Rocha, Rosana; Rosa, Bruno; Veiga, Thabata; Augusto Da Silva, Luiz; Gonçalves Geraldo, Jordana; Da Penha Morita Ananias, Maria; Nogueira Coelho, Erica; Paiva, Gabriel; Pozo, Marina; Prando, Natalia; Dada Martineli Torres, Debora; Fernanda Butinhao, Cristiani; Coelho, Erica; Renata Cubas Volpe, Luciana; Duran, Gustavo; Gomes Da Silva, Tamires Cristina; Otavio Maia Gonçalves, Luiz; Pazetto, Lucas Eduardo; Souza Duca, Luciana; Suriane Fialho, Tomás Augusto; Gheller Friedrich, Maurício André; Guerreiro, Alexandre; Mohr, Henrique; Pereira Martins, Maurer; Da Cruz Pacheco, Daiane; Macagnan, Ana Paula; De Cassia Santos, Aline; Bulle Oliveira, Acary Souza; Amaral De Andrade, Ana Carolina; Annes, Marcelo; Cavalcante Lino, Valeria; Pinto, Wladimir; Miranda, Carolina; Carrara, Fernanda; Souza, Iandra; Genge, Angela; Massie, Rami; Campbell, Natasha; Bril, Vera; Katzberg, Hans; Soltani, Mehran; Ng, Eduardo; Siddiqi, Zaeem; Phan, Celile; Blackmore, Derrick; Vohanka, Stanislav; Bednarik, Josef; Chmelikova, Magda; Cierny, Marek; Toncrova, Stanislava; Junkerova, Jana; Kurkova, Barbora; Reguliova, Katarina; Zapletalova, Olga; Pitha, Jiri; Novakova, Iveta; Tyblova, Michaela; Wolfova, Marcela; Jurajdova, Ivana; Andersen, Henning; Harbo, Thomas; Vinge, Lotte; Mogensen, Anita; Højgaard, Joan; Witting, Nanna; Autzen, Anne Mette; Pedersen, Jane; Färkkilä, Markus; Atula, Sari; Nyrhinen, Anne; Erälinna, Juha-Pekka; Laaksonen, Mikko; Oksaranta, Olli; Eriksson, Jaana; Harrison, Tuula; Desnuelle, Claude; Sacconi, Sabrina; Soriani, Marie-Hélène; Decressac, Sonia; Moutarde, Julie; Lahaut, Pauline; Solé, Guilhem; Le Masson, Gwendal; Wielanek-Bachelet, Anne-Cécile; Gaboreau, Morgane; Moreau, Caroline; Wilson, Amy; Vial, Christophe; Bouhour, Françoise; Gervais-Bernard, Helene; Merle, Hélène; Hourquin, Caroline; Lacour, Arnaud; Outteryck, Olivier; Vermersch, Patrick; Zephir, Hélène; Millois, Edouard; Deneve, Michel; Deruelle, Fabienne; Schoser, Benedikt; Wenninger, Stephan; Stangel, Martin; Alvermann, Sascha; Gingele, Stefan; Skripuletz, Thomas; Suehs, Kurt-Wolfram; Trebst, Corinna; Fricke, Karin; Papagiannopoulos, Sotirios; Bostantzopoulou, Sevasti; Vlaikidis, Nicholas; Zampaki, Martha; Papadopoulou, Nikoletta; Mitsikostas, Dimos-Dimitrios; Kasioti, Eleni; Mitropoulou, Efstathia; Charalambous, Despoina; Rozsa, Csilla; Horvath, Melinda; Lovas, Gabor; Matolcsi, Judit; Szabo, Gyorgyi; Szabadosne, Brigitta; Vecsei, Laszlo; Dezsi, Livia; Varga, Edina; Konyane, Monika; Gross, Bella; Azrilin, Olga; Greenbereg, Nelly; Bali Kuperman, Hila; Antonini, Giovanni; Garibaldi, Matteo; Morino, Stefania; Troili, Fernanda; Di Pasquale, Antonella; Filla, Alessandro; Costabile, Teresa; Marano, Enrico; Sacca, Francesco; Marsil, Angela; Puorro, Giorgia; Maestri Tassoni, Michelangelo; De Rosa, Anna; Bonanno, Silvia; Antozzi, Carlo; Maggi, Lorenzo; Campanella, Angela; Angelini, Corrado; Cudia, Paola; Pegoraro, Valentina; Pinzan, Elena; Bevilacqua, Francesca; Orrico, Daniele; Bonifati, Domenico Marco; Evoli, Amelia; Alboini, Paolo Em - 01a Articolo in rivista
rivista: LANCET NEUROLOGY (Lancet Publishing Group) pp. 976-986 - issn: 1474-4422 - wos: WOS:000415315400015 (353) - scopus: 2-s2.0-85035019720 (416)

11573/908603 - 2016 - Marked efficacy of Rituximab in multifocal motor neuropathy associated with chronic lymphocytic leukemia
Fionda, Laura; De Santis, Tiziana; Bucci, Elisabetta; Stefania, Morino; Antonella Di, Pasquale; Mauro, Francesca Romana; Antonini, Giovanni - 01a Articolo in rivista
rivista: OPEN JOURNAL OF CLINICAL & MEDICAL CASE REPORTS (Las Vegas, NV : Open Journal of Clinical and Medical Case Reports [2015-]) pp. 1-8 - issn: 2379-1039 - wos: (0) - scopus: (0)

11573/908975 - 2016 - Marked efficacy of rituximab in multifocal motor neuropathy associated with chronic lymphocytic leukemia
Fionda, Laura; Tiziana, De Santis; Elisabetta, Bucci; Stefania, Morino; Antonella Di, Pasquale; Mauro, Francesca Romana; Antonini, Giovanni - 01a Articolo in rivista
rivista: OPEN JOURNAL OF CLINICAL & MEDICAL CASE REPORTS (Las Vegas, NV : Open Journal of Clinical and Medical Case Reports [2015-]) pp. 1163-1171 - issn: 2379-1039 - wos: (0) - scopus: (0)

11573/629318 - 2014 - Cutaneous silent period recordings in demyelinating and axonal polyneuropathies
Lopergolo, D.; Isak, B.; Gabriele, M.; Onesti, Emanuela; Ceccanti, M.; Capua, G.; Fionda, L.; Biasiotta, Antonella; Di Stefano, Giulia; La Cesa, Silvia; Frasca, Vittorio; Inghilleri, Maurizio - 01a Articolo in rivista
rivista: CLINICAL NEUROPHYSIOLOGY (Elsevier Science Ireland Limited:PO Box 85, Limerick Ireland:011 353 61 709600, 011 353 61 61944, EMAIL: usinfo-f@elsevier.com, INTERNET: http://www.elsevier.com, Fax: 011 353 61 709114) pp. 1780-1789 - issn: 1388-2457 - wos: WOS:000359319800021 (15) - scopus: 2-s2.0-84938967619 (15)

© Università degli Studi di Roma "La Sapienza" - Piazzale Aldo Moro 5, 00185 Roma